Patients
17.12.22
Margaux discovering the world thanks to gene therapy
She was the first Belgian girl with the rare immunodeficiency ADA-SCID treated with the gene therapy approach developed by Telethon researchers. From the risk of a life of seclusion, she has conquered the possibility of doing whatever she likes.
10.10.19
Lorenzo wants to go far
“I can’t walk”. When you hear those words on the lips of a child below the age of three, it’s hard to turn your back and walk away. Imagine you’re the child’s parents. The words came out with the composed calmness of a fact of nature.
10.10.19
Against mitochondrial diseases together with Andrea
Knowing that the machine you need to breathe with has just one hour’s run time doesn’t make life very easy!
09.10.19
Gabriele's world
Gabriele is fast! Faster than the speed of light! On his “spiderina” – his little ‘sports car’ – he runs circles around his mum and dad, Daniela and Francesco!
27.11.18
Tommaso and his return to Normality
Tommaso was treated for ADA-SCID in February 2016 at the San Raffaele Telethon Institute in Milan (SR – Tiget).
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