A RANDOMIZED TRIAL OF DEFLAZACORT AND PREDNISONE IN DUCHENNE AND OTHER DYSTROPHIES: STUDY OF STEROIDS ACTION
- 3 Anni 1997/2000
- 123.950€ Totale Fondi
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Pubblicazioni Scientifiche
- BAILLIERES CLINICAL ENDOCRINOLOGY AND METABOLISM
DEFECTS OF FATTY-ACID OXIDATION IN MUSCLE
- LANCET
CROSS-REACTIVE PROTEIN IN DUCHENNE MUSCLE
- MUSCLE & NERVE
A multicenter, double-blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy
- MUSCLE & NERVE
Homozygous α-sarcoglycan mutation in two siblings:: One asymptomatic and one steroid-responsive mild limb-girdle muscular dystrophy patient
- NEUROLOGY
The clinical spectrum of sarcoglycanopathies
- NEUROMUSCULAR DISORDERS
Unilateral calf hypertrophy due to S1-radiculopathy
- NEUROMUSCULAR DISORDERS
PREVALENCE OF DYSTROPHIN-POSITIVE FIBERS IN 85 DUCHENNE MUSCULAR-DYSTROPHY PATIENTS
- NEUROMUSCULAR DISORDERS
DYSTROPHIN-POSITIVE MYOTUBES IN INNERVATED MUSCLE CULTURES FROM DUCHENNE AND BECKER MUSCULAR-DYSTROPHY PATIENTS
- NEUROMUSCULAR DISORDERS
Cardiac and respiratory involvement in advanced stage Duchenne muscular dystrophy
- NEUROMUSCULAR DISORDERS
Genotype-phenotype correlations of DHP receptor alpha(1)-subunit gene mutations causing hypokalemic periodic paralysis
- NEUROMUSCULAR DISORDERS
Steroids in muscular dystrophy: where do we stand?