GENE TRANSFER INTO MUSCLE

Pubblicazioni Scientifiche

• 2000 JOURNAL OF CLINICAL INVESTIGATION

  Myogenic stem cells for the therapy of primary myopathies: wishful thinking or therapeutic perspective?

• 2001 Blood

  High-level erythroid-specific gene expression in primary human and murine hematopoietic cells with self-inactivating lentiviral vectors

• 2001 NATURE

  Bone-marrow transplantation - Failure to correct murine muscular dystrophy

• 2008 EMBO REPORTS

  Genetic modification of somatic stem cells - The progress, problems and prospects of a new therapeutic technology

• 2005 HUMAN GENE THERAPY

  Competitive engraftment of hematopoietic stem cells genetically modified with a truncated erythropoietin receptor

• 2002 PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AME

  Muscle-derived hematopoietic stem cells are hematopoietic in origin

• 2001 JOURNAL OF BIOLOGICAL CHEMISTRY

  The recruitment of SOX/OCT complexes and the differential activity of HOXA1 and HOXB1 modulate the Hoxb1 auto-regulatory enhancer function

• 2003 NATURE MEDICINE

  Safety of retroviral gene marking with a truncated NGF receptor

• 2002 NEUROMUSCULAR DISORDERS

  Myogenic stem cells from the bone marrow: a therapeutic alternative for muscular dystrophy?