GENETIC REPLACEMENT IN X-LINKED MUSCULAR DYSTROPHIES: MYOBLAST TRANSFER AND GENE THERAPY
- 2 Anni 1991/1993
 - 191.089€ Totale Fondi
 
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Pubblicazioni Scientifiche
- 1995-12-04 AMERICAN JOURNAL OF MEDICAL GENETICS 
DMD AND BMD IN THE SAME FAMILY DUE TO 2 DISTINCT MUTATIONS
 - 1993-09-01 JOURNAL OF NEUROLOGY 
DYSTROPHIN ABNORMALITIES IN DUCHENNE AND BECKER DYSTROPHY CARRIERS - CORRELATION WITH CYTOSKELETAL PROTEINS AND MYOSINS
 - 1994-09-01 JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY 
A UNIQUE CASE OF DYSTROPHINOPATHY
 - 1995-10-01 JOURNAL OF THE NEUROLOGICAL SCIENCES 
DYSTROPHIN CHARACTERIZATION IN BMD PATIENTS - CORRELATION OF ABNORMAL PROTEIN WITH CLINICAL PHENOTYPE
 - 1994-10-01 MUSCLE & NERVE 
FETUS-LIKE DYSTROPHIN EXPRESSION AND OTHER CYTOSKELETAL PROTEIN ABNORMALITIES IN CENTRONUCLEAR MYOPATHIES
 - 1995-07-01 NEUROMUSCULAR DISORDERS 
LACK OF MESSENGER-RNA AND DYSTROPHIN EXPRESSION IN DMD PATIENTS 3 MONTHS AFTER MYOBLAST TRANSFER